PTC THERAPEUTICS (PTCT) Closes Sangamo Deal for Fabry Gene Therapy ST-920

PTC Therapeutics has completed its acquisition of ST-920 from Sangamo and expects to finish a rolling BLA submission for accelerated approval in Q4 2026.

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PTC Therapeutics is adding a one-time gene therapy for Fabry disease to its rare-disease pipeline.
Source: Wikimedia

PTC Therapeutics (PTCT) said it has completed the previously announced agreement with Sangamo Therapeutics to acquire ST-920, a BLA-stage, one-time administered AAV gene therapy for Fabry disease. The Warren, New Jersey company expects to complete a rolling BLA submission to the FDA seeking accelerated approval in the fourth quarter of 2026.